A humanized Smn gene containing the SMN2 nucleotide alteration in exon 7 mimics SMN2 splicing and the SMA disease phenotype

Jordan T. Gladman, Thomas W. Bebee, Chris Edwards, Xueyong Wang, Zarife Sahenk, Mark M. Rich, Dawn S. Chandler

Research output: Contribution to journalArticlepeer-review

Original languageEnglish
Article numberddq343
Pages (from-to)4239-4252
Number of pages14
JournalHuman Molecular Genetics
Volume19
Issue number21
DOIs
StatePublished - Aug 12 2010
Externally publishedYes

ASJC Scopus Subject Areas

  • Molecular Biology
  • Genetics
  • Genetics(clinical)

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