Safety and Efficacy of Long-Term Velaglucerase Alfa Therapy in Treatment-Naïve Adults with Type 1 Gaucher Disease: Results from Phase III Trials

Pilar Giraldo; Ari Zimran; Atul Mehta; Derralynn A. Hughes; Thomas N. Hangartner; Nan Wang; Gabriel M. Cohn; Eric Crombez; Deborah Elstein

doi:10.1016/j.ymgme.2013.12.097

Safety and Efficacy of Long-Term Velaglucerase Alfa Therapy in Treatment-Naïve Adults with Type 1 Gaucher Disease: Results from Phase III Trials

Pilar Giraldo, Ari Zimran, Atul Mehta, Derralynn A. Hughes, Thomas N. Hangartner, Nan Wang, Gabriel M. Cohn, Eric Crombez, Deborah Elstein

Wright State University

Research output: Contribution to conference › Presentation

Abstract

A subgroup analysis of the safety and efficacy of velaglucerase alfa in adult patients (age ≥ 18 years) with type I Gaucher disease (GD1) who were treatment-naïve at advent of trial participation is presented.

Original language	American English
DOIs	https://doi.org/10.1016/j.ymgme.2013.12.097
State	Published - Feb 1 2014
Event	Molecular Genetics and Metabolism - Duration: Feb 1 2014 → …

Conference

Conference	Molecular Genetics and Metabolism
Period	2/1/14 → …

Disciplines

Biomedical Engineering and Bioengineering
Engineering
Industrial Engineering
Operations Research, Systems Engineering and Industrial Engineering

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10.1016/j.ymgme.2013.12.097License: Unspecified

Cite this

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title = "Safety and Efficacy of Long-Term Velaglucerase Alfa Therapy in Treatment-Na{\"i}ve Adults with Type 1 Gaucher Disease: Results from Phase III Trials",

abstract = " A subgroup analysis of the safety and efficacy of velaglucerase alfa in adult patients (age ≥ 18 years) with type I Gaucher disease (GD1) who were treatment-na{\"i}ve at advent of trial participation is presented.",

author = "Pilar Giraldo and Ari Zimran and Atul Mehta and Hughes, {Derralynn A.} and Hangartner, {Thomas N.} and Nan Wang and Cohn, {Gabriel M.} and Eric Crombez and Deborah Elstein",

year = "2014",

month = feb,

day = "1",

doi = "10.1016/j.ymgme.2013.12.097",

language = "American English",

note = "Molecular Genetics and Metabolism ; Conference date: 01-02-2014",

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T1 - Safety and Efficacy of Long-Term Velaglucerase Alfa Therapy in Treatment-Naïve Adults with Type 1 Gaucher Disease: Results from Phase III Trials

AU - Giraldo, Pilar

AU - Zimran, Ari

AU - Mehta, Atul

AU - Hughes, Derralynn A.

AU - Hangartner, Thomas N.

AU - Wang, Nan

AU - Cohn, Gabriel M.

AU - Crombez, Eric

AU - Elstein, Deborah

PY - 2014/2/1

Y1 - 2014/2/1

N2 - A subgroup analysis of the safety and efficacy of velaglucerase alfa in adult patients (age ≥ 18 years) with type I Gaucher disease (GD1) who were treatment-naïve at advent of trial participation is presented.

AB - A subgroup analysis of the safety and efficacy of velaglucerase alfa in adult patients (age ≥ 18 years) with type I Gaucher disease (GD1) who were treatment-naïve at advent of trial participation is presented.

UR - https://corescholar.libraries.wright.edu/bie/128

U2 - 10.1016/j.ymgme.2013.12.097

DO - 10.1016/j.ymgme.2013.12.097

M3 - Presentation

T2 - Molecular Genetics and Metabolism

Y2 - 1 February 2014

ER -

Safety and Efficacy of Long-Term Velaglucerase Alfa Therapy in Treatment-Naïve Adults with Type 1 Gaucher Disease: Results from Phase III Trials

Abstract

Conference

Disciplines

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