Safety and Efficacy of Long-Term Velaglucerase Alfa Therapy in Treatment-Naïve Adults with Type 1 Gaucher Disease: Results from Phase III Trials

Pilar Giraldo; Ari Zimran; Atul Mehta; Derralynn A. Hughes; Thomas N. Hangartner; Nan Wang; Gabriel M. Cohn; Eric Crombez; Deborah Elstein

doi:10.1016/j.ymgme.2013.12.097

Safety and Efficacy of Long-Term Velaglucerase Alfa Therapy in Treatment-Naïve Adults with Type 1 Gaucher Disease: Results from Phase III Trials

Pilar Giraldo, Ari Zimran, Atul Mehta, Derralynn A. Hughes, Thomas N. Hangartner, Nan Wang, Gabriel M. Cohn, Eric Crombez, Deborah Elstein

Research output: Contribution to conference › Presentation

Abstract

A subgroup analysis of the safety and efficacy of velaglucerase alfa in adult patients (age ≥ 18 years) with type I Gaucher disease (GD1) who were treatment-naïve at advent of trial participation is presented.

Original language	American English
DOIs	https://doi.org/10.1016/j.ymgme.2013.12.097
State	Published - Feb 1 2014
Event	Molecular Genetics and Metabolism - Duration: Feb 1 2014 → …

Conference

Conference	Molecular Genetics and Metabolism
Period	2/1/14 → …

Disciplines

Biomedical Engineering and Bioengineering
Engineering
Industrial Engineering
Operations Research, Systems Engineering and Industrial Engineering

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10.1016/j.ymgme.2013.12.097License: Unspecified

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title = "Safety and Efficacy of Long-Term Velaglucerase Alfa Therapy in Treatment-Na{\"i}ve Adults with Type 1 Gaucher Disease: Results from Phase III Trials",

abstract = " A subgroup analysis of the safety and efficacy of velaglucerase alfa in adult patients (age ≥ 18 years) with type I Gaucher disease (GD1) who were treatment-na{\"i}ve at advent of trial participation is presented.",

author = "Pilar Giraldo and Ari Zimran and Atul Mehta and Hughes, \{Derralynn A.\} and Hangartner, \{Thomas N.\} and Nan Wang and Cohn, \{Gabriel M.\} and Eric Crombez and Deborah Elstein",

year = "2014",

month = feb,

day = "1",

doi = "10.1016/j.ymgme.2013.12.097",

language = "American English",

note = "Molecular Genetics and Metabolism ; Conference date: 01-02-2014",

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T1 - Safety and Efficacy of Long-Term Velaglucerase Alfa Therapy in Treatment-Naïve Adults with Type 1 Gaucher Disease: Results from Phase III Trials

AU - Giraldo, Pilar

AU - Zimran, Ari

AU - Mehta, Atul

AU - Hughes, Derralynn A.

AU - Hangartner, Thomas N.

AU - Wang, Nan

AU - Cohn, Gabriel M.

AU - Crombez, Eric

AU - Elstein, Deborah

PY - 2014/2/1

Y1 - 2014/2/1

N2 - A subgroup analysis of the safety and efficacy of velaglucerase alfa in adult patients (age ≥ 18 years) with type I Gaucher disease (GD1) who were treatment-naïve at advent of trial participation is presented.

AB - A subgroup analysis of the safety and efficacy of velaglucerase alfa in adult patients (age ≥ 18 years) with type I Gaucher disease (GD1) who were treatment-naïve at advent of trial participation is presented.

UR - https://corescholar.libraries.wright.edu/bie/128

U2 - 10.1016/j.ymgme.2013.12.097

DO - 10.1016/j.ymgme.2013.12.097

M3 - Presentation

T2 - Molecular Genetics and Metabolism

Y2 - 1 February 2014

ER -

Safety and Efficacy of Long-Term Velaglucerase Alfa Therapy in Treatment-Naïve Adults with Type 1 Gaucher Disease: Results from Phase III Trials

Abstract

Conference

Disciplines

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